FDA Approves Gene Therapy

Share this story on:

Share on facebook
Share on twitter
Share on linkedin

WASHINGTON — Opening a new era in cancer care, U.S. health officials on Wednesday approved a breakthrough treatment that genetically engineers patients’ own blood cells into an army of assassins to seek and destroy childhood leukemia.

The Food and Drug Administration called the approval historic, the first gene therapy to hit the U.S. market. Made from scratch for every patient, it’s one of a wave of “living drugs” under development to fight additional blood cancers and other tumors, too.

Novartis Pharmaceuticals set the price for its one-time infusion of so-called “CAR-T cells” at $475,000, but said there would be no charge for patients who didn’t show a response within a month.

“This is a brand new way of treating cancer,” said Dr. Stephan Grupp of Children’s Hospital of Philadelphia, who treated the first child with CAR-T cell therapy — a girl who’d been near death but now is cancer-free for five years and counting. “That’s enormously exciting.”

CAR-T treatment uses gene therapy techniques not to fix disease-causing genes but to turbocharge T cells, immune system soldiers that cancer too often can evade. Researchers filter those cells from a patient’s blood, reprogram them to harbor a “chimeric antigen receptor” or CAR that zeroes in on cancer, and grow hundreds of millions of copies. Returned to the patient, the revved-up cells can continue multiplying to fight disease for months or years.

Teresa
Teresa

Recent Posts

Teresa

January 2022

We will be closed the week of Monday, Jan. 24th – 28th.  Call 812-558-5383 to leave a message so we can call you back on

Read More »
Teresa

2022 Winter Hours

Our office will be open 9am to 4pm, beginning January 20th through March 11th this year.  Personal appointments are still available outside of these hours! 

Read More »
Teresa

Update: Full Vax Against COVID

Update:  As of 4/30/21: Indiana= 1.76 million residents.  26.25% of state population. Kentucky= 1.40 million residents.  31.34% of state population. Florida= 6.13 million residents.  28.57%

Read More »
Teresa

Indiana Update

Over 954,000 people in the state of Indiana have been fully vaccinated against COVID-19. There are 548 people in Indiana hospitals because of COVID-19; and

Read More »

copyright 2020 Evansville Insurance Center